Think back to that basic biology class you took in high school. You probably learned about organelles, those little “organs” ...

This came after Takeda Biopharmaceuticals presented the proposal for an update in the package insert regarding home infusion ...

MIPLYFFA has also been shown to reduce unesterified cholesterol in the lysosomes of human NPC fibroblasts. The clinical significance of these findings is not fully understood. MIPLYFFA was granted ...

The expert panel further added, "The safety and efficacy data are to be deliberated in the presence of an independent expert ...

Alexion has gained FDA approval for Kanuma, its treatment for the rare disease lysosomal acid lipase (LAL ... and used both its human and veterinary health divisions. Alexion says the GE chickens ...

Q3 2024 Total Revenue of $141.5M, a 37% Increase Year-over-Year Galafold®Q3 Revenue of $120.4M, up 20% Year-over-Year PRINCETON, N.J., Nov. 06, 2024 (GLOBE NEWSWIRE) -- Amicus Therapeutics (Nasdaq: ...

NEW HAVEN, Conn., Oct. 30, 2024 (GLOBE NEWSWIRE) -- Arvinas, Inc. (Nasdaq: ARVN), a clinical-stage biotechnology company creating a new class of drugs based on targeted protein degradation, today ...

Gaucher disease (GD; MIM230800) is a lysosomal storage disease caused by glucocerebrosidase ... the adverse event was related to the medical treatment. The GBA (NM_000157) human cDNA clone was ...

This review explores the role of lysosomal stress in pancreatic diseases, particularly diabetes mellitus. Lysosomes, crucial ...

POLK expression in neurons and report an important observation that POLK exhibits an age-dependent change in subcellular localization, from the nucleus in young tissue to the cytoplasm in old tissue.